Therapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing

  1. Hatanaka, F.
  2. Suzuki, K.
  3. Shojima, K.
  4. Yu, J.
  5. Takahashi, Y.
  6. Sakamoto, A.
  7. Prieto, J.
  8. Shokhirev, M.
  9. Nuñez Delicado, E.
  10. Rodriguez Esteban, C.
  11. Izpisua Belmonte, J.C.
Revue:
Nature Communications

ISSN: 2041-1723

Année de publication: 2024

Volumen: 15

Número: 1

Type: Article

DOI: 10.1038/S41467-024-50095-5 GOOGLE SCHOLAR lock_openAccès ouvert editor