Therapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing

  1. Hatanaka, F.
  2. Suzuki, K.
  3. Shojima, K.
  4. Yu, J.
  5. Takahashi, Y.
  6. Sakamoto, A.
  7. Prieto, J.
  8. Shokhirev, M.
  9. Nuñez Delicado, E.
  10. Rodriguez Esteban, C.
  11. Izpisua Belmonte, J.C.
Aldizkaria:
Nature Communications

ISSN: 2041-1723

Argitalpen urtea: 2024

Alea: 15

Zenbakia: 1

Mota: Artikulua

DOI: 10.1038/S41467-024-50095-5 GOOGLE SCHOLAR lock_openSarbide irekia editor