Therapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing
- Hatanaka, F.
- Suzuki, K.
- Shojima, K.
- Yu, J.
- Takahashi, Y.
- Sakamoto, A.
- Prieto, J.
- Shokhirev, M.
- Nuñez Delicado, E.
- Rodriguez Esteban, C.
- Izpisua Belmonte, J.C.
Journal:
Nature Communications
ISSN: 2041-1723
Year of publication: 2024
Volume: 15
Issue: 1
Type: Article