Therapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing

  1. Hatanaka, F.
  2. Suzuki, K.
  3. Shojima, K.
  4. Yu, J.
  5. Takahashi, Y.
  6. Sakamoto, A.
  7. Prieto, J.
  8. Shokhirev, M.
  9. Nuñez Delicado, E.
  10. Rodriguez Esteban, C.
  11. Izpisua Belmonte, J.C.
Journal:
Nature Communications

ISSN: 2041-1723

Year of publication: 2024

Volume: 15

Issue: 1

Type: Article

DOI: 10.1038/S41467-024-50095-5 GOOGLE SCHOLAR lock_openOpen access editor