Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model
- Overby, S.J.
- Cerro-Herreros, E.
- González-Martínez, I.
- Varela, M.A.
- Seoane-Miraz, D.
- Jad, Y.
- Raz, R.
- Møller, T.
- Pérez-Alonso, M.
- Wood, M.J.
- Llamusí, B.
- Artero, R.
Aldizkaria:
Molecular Therapy - Nucleic Acids
ISSN: 2162-2531
Argitalpen urtea: 2022
Alea: 27
Orrialdeak: 1146-1155
Mota: Artikulua