Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model

  1. Overby, S.J.
  2. Cerro-Herreros, E.
  3. González-Martínez, I.
  4. Varela, M.A.
  5. Seoane-Miraz, D.
  6. Jad, Y.
  7. Raz, R.
  8. Møller, T.
  9. Pérez-Alonso, M.
  10. Wood, M.J.
  11. Llamusí, B.
  12. Artero, R.
Journal:
Molecular Therapy - Nucleic Acids

ISSN: 2162-2531

Year of publication: 2022

Volume: 27

Pages: 1146-1155

Type: Article

DOI: 10.1016/J.OMTN.2022.02.003 GOOGLE SCHOLAR lock_openOpen access editor