Publicaciones en colaboración con investigadores/as de Boston Children's Hospital (3)

2021

  1. Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy

    Journal of Comparative Effectiveness Research, Vol. 10, Núm. 18, pp. 1337-1347

2018

  1. DEFLAZACORT VERSUS PREDNISONE/PREDNISOLONE FOR MAINTAINING MOTOR FUNCTION AND DELAYING LOSS OF AMBULATION: A POST HOC ANALYSIS FROM THE ACT DMD TRIAL

    Muscle and Nerve, Vol. 58, Núm. 5, pp. 639-645

2014

  1. Novel Mutations Widen the Phenotypic Spectrum of Slow Skeletal/β-Cardiac Myosin (MYH7) Distal Myopathy

    Human Mutation, Vol. 35, Núm. 7, pp. 868-879