JUAN J
VILCHEZ PADILLA
TITULAR DE UNIVERSIDAD
University of California Los Angeles
Los Ángeles, Estados UnidosPublicaciones en colaboración con investigadores/as de University of California Los Angeles (3)
2021
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Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy
Journal of Comparative Effectiveness Research, Vol. 10, Núm. 18, pp. 1337-1347
2018
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DEFLAZACORT VERSUS PREDNISONE/PREDNISOLONE FOR MAINTAINING MOTOR FUNCTION AND DELAYING LOSS OF AMBULATION: A POST HOC ANALYSIS FROM THE ACT DMD TRIAL
Muscle and Nerve, Vol. 58, Núm. 5, pp. 639-645
2017
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Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
The Lancet, Vol. 390, Núm. 10101, pp. 1489-1498