Publicaciones en colaboración con investigadores/as de Tel Aviv University (2)

2022

  1. Efficacy and Safety of Vamorolone vs Placebo and Prednisone among Boys with Duchenne Muscular Dystrophy: A Randomized Clinical Trial

    JAMA Neurology, Vol. 79, Núm. 10, pp. 1005-1014

2020

  1. Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy

    Journal of Comparative Effectiveness Research, Vol. 9, Núm. 14, pp. 973-984