ARIADNA
BARGIELA SCHONBRUNN
INVEST DOCT UV SENIOR
Instituto de Investigación Sanitaria La Fe
Valencia, EspañaPublicacions en col·laboració amb investigadors/es de Instituto de Investigación Sanitaria La Fe (5)
2024
-
Msi2 enhances muscle dysfunction in a myotonic dystrophy type 1 mouse model
Biomedical Journal, Vol. 47, Núm. 4
-
Therapeutic potential of oleic acid supplementation in myotonic dystrophy muscle cell models
Biological Research, Vol. 57, Núm. 1
2023
-
CRISPR-Cas9 editing of a TNPO3 mutation in a muscle cell model of limb-girdle muscular dystrophy type D2
Molecular Therapy - Nucleic Acids, Vol. 31, pp. 324-338
2022
-
Development of potent tripodal G-quadruplex DNA binders and their efficient delivery to cancer cells by aptamer functionalised liposomes
Organic and Biomolecular Chemistry, Vol. 21, Núm. 5, pp. 1000-1007
2021
-
Musashi-2 contributes to myotonic dystrophy muscle dysfunction by promoting excessive autophagy through miR-7 biogenesis repression
Molecular Therapy - Nucleic Acids, Vol. 25, pp. 652-667