JUAN MANUEL
FERNANDEZ COSTA
INVEST CONT VALi+d
MANUEL
PEREZ ALONSO
CATEDRÁTICO/A DE UNIVERSIDAD
MANUEL PEREZ ALONSO-rekin lankidetzan egindako argitalpenak (6)
2023
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BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSALR Mice
Pharmaceutics, Vol. 15, Núm. 4
2021
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Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy
Molecular Therapy - Nucleic Acids, Vol. 26, pp. 174-191
2018
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MiR-23b and miR-218 silencing increase Muscleblind-like expression and alleviate myotonic dystrophy phenotypes in mammalian models
Nature Communications, Vol. 9, Núm. 1
2017
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Myotonic dystrophy: candidate small molecule therapeutics
Drug Discovery Today, Vol. 22, Núm. 11, pp. 1740-1748
2016
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Six serum miRNAs fail to validate as myotonic dystrophy type 1 biomarkers
PLoS ONE, Vol. 11, Núm. 2
2013
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Expanded CTG repeats trigger miRNA alterations in Drosophila that are conserved in myotonic dystrophy type 1 patients
Human Molecular Genetics, Vol. 22, Núm. 4, pp. 704-716