RUBEN DARIO
ARTERO ALLEPUZ
CATEDRÁTICO/A DE UNIVERSIDAD
Publications (85) Publications de RUBEN DARIO ARTERO ALLEPUZ
2024
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Msi2 enhances muscle dysfunction in a myotonic dystrophy type 1 mouse model
Biomedical Journal, Vol. 47, Núm. 4
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Taurine activates the AKT-mTOR axis to restore muscle mass and contractile strength in human 3D in vitro models of steroid myopathy
Disease models & mechanisms, Vol. 17, Núm. 4
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Therapeutic potential of oleic acid supplementation in myotonic dystrophy muscle cell models
Biological Research, Vol. 57, Núm. 1
2023
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BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSALR Mice
Pharmaceutics, Vol. 15, Núm. 4
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CRISPR-Cas9 editing of a TNPO3 mutation in a muscle cell model of limb-girdle muscular dystrophy type D2
Molecular Therapy - Nucleic Acids, Vol. 31, pp. 324-338
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Natural Compound Boldine Lessens Myotonic Dystrophy Type 1 Phenotypes in DM1 Drosophila Models, Patient-Derived Cell Lines, and HSALR Mice
International Journal of Molecular Sciences, Vol. 24, Núm. 12
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Neuroprotective properties of queen bee acid by autophagy induction
Cell Biology and Toxicology, Vol. 39, Núm. 3, pp. 751-770
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Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression
Molecular Therapy - Nucleic Acids, Vol. 34
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Quantitative magnetic resonance imaging assessment of muscle composition in myotonic dystrophy mice
Scientific Reports, Vol. 13, Núm. 1
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The myotonic dystrophy type 1 drug development pipeline: 2022 edition
Drug Discovery Today, Vol. 28, Núm. 3
2022
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Deciphering the Complex Molecular Pathogenesis of Myotonic Dystrophy Type 1 through Omics Studies
International Journal of Molecular Sciences, Vol. 23, Núm. 3
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Moxifloxacin rescues SMA phenotypes in patient-derived cells and animal model
Cellular and Molecular Life Sciences, Vol. 79, Núm. 8
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Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model
Molecular Therapy - Nucleic Acids, Vol. 27, pp. 1146-1155
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Rapid Determination of MBNL1 Protein Levels by Quantitative Dot Blot for the Evaluation of Antisense Oligonucleotides in Myotonic Dystrophy Myoblasts
Methods in molecular biology (Clifton, N.J.), Vol. 2434, pp. 207-215
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Role of miRNAs in muscle atrophy: the myotonic dystrophy paradigm
MicroRNA: From Bench to Bedside (Elsevier), pp. 331-362
2021
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Bioengineered in vitro 3D model of myotonic dystrophy type 1 human skeletal muscle
Biofabrication, Vol. 13, Núm. 3
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Defined d-hexapeptides bind CUG repeats and rescue phenotypes of myotonic dystrophy myotubes in a Drosophila model of the disease
Scientific Reports, Vol. 11, Núm. 1
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Guidelines for the use and interpretation of assays for monitoring autophagy (4th edition)1
Autophagy, Vol. 17, Núm. 1, pp. 1-382
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Inhibition of autophagy rescues muscle atrophy in a LGMDD2 Drosophila model
FASEB Journal, Vol. 35, Núm. 10
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Musashi-2 contributes to myotonic dystrophy muscle dysfunction by promoting excessive autophagy through miR-7 biogenesis repression
Molecular Therapy - Nucleic Acids, Vol. 25, pp. 652-667