ESTEFANIA
CERRO HERREROS
INVEST CONT VALi+d
Instituto de Investigación Sanitaria Fundación para la Investigación del Hospital Clínico de Valencia
Valencia, EspañaPublications in collaboration with researchers from Instituto de Investigación Sanitaria Fundación para la Investigación del Hospital Clínico de Valencia (2)
2022
-
Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model
Molecular Therapy - Nucleic Acids, Vol. 27, pp. 1146-1155
2021
-
Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy
Molecular Therapy - Nucleic Acids, Vol. 26, pp. 174-191