ESTEFANIA
CERRO HERREROS
INVEST CONT VALi+d
JUAN MANUEL
FERNANDEZ COSTA
INVEST CONT VALi+d
Publicaciones en las que colabora con JUAN MANUEL FERNANDEZ COSTA (6)
2023
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BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSALR Mice
Pharmaceutics, Vol. 15, Núm. 4
2021
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Bioengineered in vitro 3D model of myotonic dystrophy type 1 human skeletal muscle
Biofabrication, Vol. 13, Núm. 3
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Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy
Molecular Therapy - Nucleic Acids, Vol. 26, pp. 174-191
2018
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MiR-23b and miR-218 silencing increase Muscleblind-like expression and alleviate myotonic dystrophy phenotypes in mammalian models
Nature Communications, Vol. 9, Núm. 1
2016
2015
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Increased autophagy and apoptosis contribute to muscle atrophy in a myotonic dystrophy type 1 Drosophila model
DMM Disease Models and Mechanisms, Vol. 8, Núm. 7, pp. 679-690