Grupo de investigación en enfermedades raras respiratorias
ERR
Instituto de Biomedicina de Valencia
Valencia, EspañaPublicacións en colaboración con investigadores/as de Instituto de Biomedicina de Valencia (6)
2016
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Human AAT gene transfer to pig liver improved by using a perfusion isolated organ endovascular procedure
European Radiology, Vol. 26, Núm. 1, pp. 95-102
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Studying closed hydrodynamic models of "in vivo" DNA perfusion in pig liver for gene therapy translation to humans
PLoS ONE, Vol. 11, Núm. 10
2014
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Low RNA translation activit limits the efficacy of hydrodynamic gene transfer to pig liver in vivo
Journal of Gene Medicine, Vol. 16, Núm. 7-8, pp. 179-192
2013
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Lafora disease fibroblasts exemplify the molecular interdependence between thioredoxin 1 and the proteasome in mammalian cells
Free Radical Biology and Medicine, Vol. 65, pp. 347-359
2011
2005
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Hydrodynamic liver gene transfer mechanism involves transient sinusoidal blood stasis and massive hepatocyte endocytic vesicles
Gene Therapy, Vol. 12, Núm. 11, pp. 927-935