Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy: A Randomized Controlled Trial

  1. Dang, U.J.
  2. Damsker, J.M.
  3. Guglieri, M.
  4. Clemens, P.R.
  5. Perlman, S.J.
  6. Smith, E.C.
  7. Horrocks, I.
  8. Finkel, R.S.
  9. Mah, J.K.
  10. Deconinck, N.
  11. Goemans, N.M.
  12. Haberlová, J.
  13. Straub, V.
  14. Mengle-Gaw, L.
  15. Schwartz, B.D.
  16. Harper, A.
  17. Shieh, P.B.
  18. De Waele, L.
  19. Castro, D.
  20. Yang, M.L.
  21. Ryan, M.M.
  22. McDonald, C.M.
  23. Tulinius, M.
  24. Webster, R.I.
  25. McMillan, H.J.
  26. Kuntz, N.
  27. Rao, V.K.
  28. Baranello, G.
  29. Spinty, S.
  30. Childs, A.-M.
  31. Sbrocchi, A.M.
  32. Selby, K.A.
  33. Monduy, M.
  34. Nevo, Y.
  35. Vilchez, J.J.
  36. Nascimento-Osorio, A.
  37. Niks, E.H.
  38. De Groot, I.J.M.
  39. Katsalouli, M.
  40. Van Den Anker, J.N.
  41. Ward, L.M.
  42. Leinonen, M.
  43. D'Alessandro, A.L.
  44. Hoffman, E.P.
  45. Show all authors +
Journal:
Neurology

ISSN: 1526-632X,  0028-3878

Year of publication: 2024

Volume: 102

Issue: 5

Type: Article

DOI: 10.1212/WNL.0000000000208112 GOOGLE SCHOLAR lock_openOpen access editor
Data source: Scopus