Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression
- González-Martínez, I.
- Cerro-Herreros, E.
- Moreno, N.
- García-Rey, A.
- Espinosa-Espinosa, J.
- Carrascosa-Sàez, M.
- Piqueras-Losilla, D.
- Arzumanov, A.
- Seoane-Miraz, D.
- Jad, Y.
- Raz, R.
- Wood, M.J.
- Varela, M.A.
- Llamusí, B.
- Artero, R.
Journal:
Molecular Therapy - Nucleic Acids
ISSN: 2162-2531
Year of publication: 2023
Volume: 34
Type: Article