BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSALR Mice
- Overby, S.J.
- Cerro-Herreros, E.
- Espinosa-Espinosa, J.
- González-Martínez, I.
- Moreno, N.
- Fernández-Costa, J.M.
- Balaguer-Trias, J.
- Ramón-Azcón, J.
- Pérez-Alonso, M.
- Møller, T.
- Llamusí, B.
- Artero, R.
Journal:
Pharmaceutics
ISSN: 1999-4923
Year of publication: 2023
Volume: 15
Issue: 4
Type: Article