Adeno-associated viral vector serotype 9-based gene therapy for Niemann-Pick disease type A
- Samaranch, L.
- Pérez-Cañamás, A.
- Soto-Huelin, B.
- Sudhakar, V.
- Jurado-Arjona, J.
- Hadaczek, P.
- Ávila, J.
- Bringas, J.R.
- Casas, J.
- Chen, H.
- He, X.
- Schuchman, E.H.
- Cheng, S.H.
- Forsayeth, J.
- Bankiewicz, K.S.
- Ledesma, M.D.
ISSN: 1946-6242, 1946-6234
Any de publicació: 2019
Volum: 11
Número: 506
Tipus: Article