CRISPR-Cas9 editing of a TNPO3 mutation in a muscle cell model of limb-girdle muscular dystrophy type D2
- Poyatos-García, J.
- Blázquez-Bernal, Á.
- Selva-Giménez, M.
- Bargiela, A.
- Espinosa-Espinosa, J.
- Vázquez-Manrique, R.P.
- Bigot, A.
- Artero, R.
- Vilchez, J.J.
Journal:
Molecular Therapy - Nucleic Acids
ISSN: 2162-2531
Year of publication: 2023
Volume: 31
Pages: 324-338
Type: Article